Life-changing cystic fibrosis treatment wins US$3-million Breakthrough Prize
https://www.nature.com/articles/d41586-023-02890-1
Discussion: https://news.ycombinator.com/item?id=37535537

* triple-drug combination Trikafta helps 90% of people w. cystic fibrosis
* inherited disorder affecting lungs, other organs
* mutations in gene that makes the cystic fibrosis transmembrane conductance regulator protein (CFTR)
* involved in production of mucus, sweat, other fluids

#CysticFibrosis #Trikafta #disease #medicine #BreakthroughPrize #CFTR